Gene therapy approved

• Autores: Andy Coghlan
• Localización: New scientist, ISSN 0262-4079, Nº. 3068, 2016, pág. 8
• Idioma: inglés
• Texto completo no disponible (Saber más ...)
• Resumen

  • They nearly lost him twice, says Kelly Gillion of her son Zeus, who was diagnosed with the potentially fatal condition ADA-SCID in the first weeks of his life. Until now the only commercial treatment for the condition has been a bone marrow transplant, and many die before a donor is found. But last week, a gene therapy to treat it was rubber-stamped for approval by a committee of the European Medicines Agency, potentially giving all patients in Europe access to a treatment that enables them to build lifelong immune systems with the help of transplanted genes